National celebrity Bill Nye “the Science Guy” returns to his lab to help a local patient advocacy nonprofit spread awareness ...

Schizophrenia (SZ) and Autism Spectrum Disorders (ASD) are two distinct heterogenous disorders that despite having a ...

A Columbus family is on a mission to find a cure for a rare genetic disorder and Saturday morning was their third annual Hope With Lo 5k. “We believe that hope isn’t ...

Kangaroo Island koalas appear safe, but genetic studies reveal hidden risks. Their survival depends on action now.

A pioneering gene therapy has successfully slowed the progression of Huntington’s disease by 75% in patients after three ...

Researchers have developed a new lipid for delivering mRNA that is safer and more effective than current technologies. By ...

Inherited heart conditions place millions of children at risk from birth. Up to 80% of premature cardiovascular deaths are ...

Huntington's Disease is a rare genetic disorder affecting more than 40,000 people in the U.S. It causes physical, mental, and ...

Preliminary results from a small trial offer the clearest evidence yet that the brain disease’s progression can be slowed.

Ahn has studied SON since the early 2000s. After the discovery of ZTTK, she co-founded the ZTTK SON-Shine Foundation in 2021 ...

New research from the Arnold School's Department of Epidemiology and Biostatistics has found disparities in mortality rates ...

An experimental gene therapy was found to slow the progression of Huntington’s disease in a “pivotal” study, according to drugmaker uniQure, marking a major step toward a potential first genetic ...